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Shortcast: Comparison of subcutaneous and intravenous moss-aGal in Fabry disease mouse model

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Manage episode 379248530 series 3001064
Konten disediakan oleh JIMD Podcasts and Journal of Inherited Metabolic Disease. Semua konten podcast termasuk episode, grafik, dan deskripsi podcast diunggah dan disediakan langsung oleh JIMD Podcasts and Journal of Inherited Metabolic Disease atau mitra platform podcast mereka. Jika Anda yakin seseorang menggunakan karya berhak cipta Anda tanpa izin, Anda dapat mengikuti proses yang diuraikan di sini https://id.player.fm/legal.
Enzyme Replacement Therapy (ERT) has changed the course of several lysosomal storage disorders but regular, intravenous administration is not without its issues. In this latest Shortcast, Dr Paulina Dabrowska-Schlepp describes her group's work to develop subcutaneous ERT for Fabry Disease. Comparison of efficacy between subcutaneous and intravenous application of moss-aGal in the mouse model of Fabry disease Paulina Dabrowska-Schlepp, et al https://doi.org/10.1002/jmd2.12393
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188 episode

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Manage episode 379248530 series 3001064
Konten disediakan oleh JIMD Podcasts and Journal of Inherited Metabolic Disease. Semua konten podcast termasuk episode, grafik, dan deskripsi podcast diunggah dan disediakan langsung oleh JIMD Podcasts and Journal of Inherited Metabolic Disease atau mitra platform podcast mereka. Jika Anda yakin seseorang menggunakan karya berhak cipta Anda tanpa izin, Anda dapat mengikuti proses yang diuraikan di sini https://id.player.fm/legal.
Enzyme Replacement Therapy (ERT) has changed the course of several lysosomal storage disorders but regular, intravenous administration is not without its issues. In this latest Shortcast, Dr Paulina Dabrowska-Schlepp describes her group's work to develop subcutaneous ERT for Fabry Disease. Comparison of efficacy between subcutaneous and intravenous application of moss-aGal in the mouse model of Fabry disease Paulina Dabrowska-Schlepp, et al https://doi.org/10.1002/jmd2.12393
  continue reading

188 episode

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